Rare Diseases Weekly News - June 12th 2025
🔬 Rare Diseases Update: Orphan Drug Wins, Genomic Breakthroughs, Global…
Rare Diseases Weekly News - June 5th 2025
🔬 Rare Diseases Update: Orphan Drug Designations, Gene Editing Breakthroughs,…
Cell and Gene Therapy Weekly News - June 5th 2025
This Week in Gene & Cell Therapy: Breakthrough Trials, Fast Track…
Cell and Gene Therapy Weekly News - May 29th 2025
This Week in Gene & Cell Therapy: Clinical Trial Expansions, Rare Disease…
Rare Diseases Weekly News - May 29th 2025
🔬 Rare Diseases Update: Orphan Drug Designations, Gene Therapies, Diagnostic…
Rare Diseases Weekly News - May 22nd 2025
🔬 Rare Diseases Update: CRISPR Therapy, SCA, ENPP1 Deficiency, Gene Therapy…
Cell and Gene Therapy Weekly News - May 22nd 2025
This Week in Gene & Cell Therapy: Personalized CRISPR, FDA Clearances, and…
Rare Diseases Weekly News - May 15th 2025
🔬 Discover the latest breakthroughs in rare disease research from this week’s…
Rare Diseases Weekly News - May 8th 2025
🔬 Discover the latest breakthroughs in rare disease research from this week’s…
How can we address challenges in rare disease drug development?
It is estimated that rare diseases affect more than 400 million people…
