Rare Disease Today—October 30, 2025
Explore this week’s Rare Diseases highlights, including new developments,…
Respiratory Weekly News - August 29th 2025
This Week in Respiratory Health: Breakthroughs in IPF, CF, COPD, MDR-TB, and…
Neuroscience Weekly News - August 13th 2025
🧠 This Week in Neuroscience: Pediatric Migraine Breakthrough, First MS CAR…
Neuroscience Weekly News - August 6th 2025
🧠 This Week in Neuroscience: MS Genetics Breakthrough, $372.5M CNS Funding, AI…
Cell and Gene Therapy Weekly News - June 5th 2025
This Week in Gene & Cell Therapy: Breakthrough Trials, Fast Track…
Cell and Gene Therapy Weekly News - May 29th 2025
This Week in Gene & Cell Therapy: Clinical Trial Expansions, Rare Disease…
Cell and Gene Therapy Weekly News - May 22nd 2025
This Week in Gene & Cell Therapy: Personalized CRISPR, FDA Clearances, and…
How can we address challenges in rare disease drug development?
It is estimated that rare diseases affect more than 400 million people…
