Rare Disease news

Rare Disease Today—October 23, 2025

This week’s rare disease news delivers the latest regulatory updates, and…


Rare Disease news

Rare Diseases Weekly News - June 26th 2025

🧬 This Week in Rare Diseases: Genome Testing, First Approvals, Global…


Rare Disease news

Rare Diseases Weekly News - May 22nd 2025

🔬 Rare Diseases Update: CRISPR Therapy, SCA, ENPP1 Deficiency, Gene Therapy…


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