Rare Disease news

Rare Disease Video Recap—January 29, 2026

This biweekly Rare Disease Video Recap highlights significant regulatory…


Rare Disease news

Rare Diseases Today—January 29, 2026

This week's rare disease updates focus on significant regulatory approvals,…


Rare Disease news

Rare Disease Today—October 23, 2025

This week’s rare disease news delivers the latest regulatory updates, and…


Rare Disease news

Rare Diseases Weekly News - June 26th 2025

🧬 This Week in Rare Diseases: Genome Testing, First Approvals, Global…


Rare Disease news

Rare Diseases Weekly News - May 22nd 2025

🔬 Rare Diseases Update: CRISPR Therapy, SCA, ENPP1 Deficiency, Gene Therapy…


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