Rare Disease news

Rare Diseases Weekly News - May 1st 2025

This Week in Rare Disease Breakthroughs 🧬 | Pivotal Approvals, New Orphan Drug…


Rare Disease news

Rare Diseases Weekly News - April 24th 2025

This Week in Rare Disease Breakthroughs 🧬 | Gene Therapies, Drug Approvals…


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