Rare Diseases Weekly News - September 30th 2025
🧬 This Week in Rare Diseases: FDA Label Expansion, Accelerated Approvals, RNA…
Neuroscience Weekly News - April 23rd 2025
Next-Level Neuroscience Innovations: Digital Migraine Therapy, EU Alzheimer’s…
How can we address challenges in rare disease drug development?
It is estimated that rare diseases affect more than 400 million people…


