Rare Disease news

Rare Diseases Weekly News - September 30th 2025

🧬 This Week in Rare Diseases: FDA Label Expansion, Accelerated Approvals, RNA…


Neuroscience

Neuroscience Weekly News - April 23rd 2025

Next-Level Neuroscience Innovations: Digital Migraine Therapy, EU Alzheimer’s…


Rare disease drug development challenges

How can we address challenges in rare disease drug development?

It is estimated that rare diseases affect more than 400 million people…


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