Rare Disease news

Rare Diseases Weekly News - July 31st 2025

🧬 This Week in Rare Diseases: FDA Leadership, Gene Therapy Safety, New Drug…


Rare Disease news

Rare Diseases Weekly News - July 24th 2025

🧬 This Week in Rare Diseases: Breakthrough Therapies, AI Innovations,…


Rare Disease news

Rare Diseases Weekly News - July 17th 2025

🧬 This Week in Rare Diseases: Global Court Win, Breakthrough Therapies, AI…


Rare Disease news

Rare Diseases Weekly News - July 10th 2025

🧬 This Week in Rare Diseases: Global Policy Shifts, FDA Approvals, New Gene…


Rare Disease news

Rare Diseases Weekly News - July 3rd 2025

🧬 This Week in Rare Diseases: First MAS Approval, AI-Powered Diagnostics,…


Rare Disease news

Rare Diseases Weekly News - June 26th 2025

🧬 This Week in Rare Diseases: Genome Testing, First Approvals, Global…


Rare Disease news

Rare Diseases Weekly News - June 19th 2025

🧬 This Week in Rare Diseases: Breakthroughs, Designations & Policy Shifts!…


Rare Disease news

Rare Diseases Weekly News - June 12th 2025

🔬 Rare Diseases Update: Orphan Drug Wins, Genomic Breakthroughs, Global…


Rare Disease news

Rare Diseases Weekly News - June 5th 2025

🔬 Rare Diseases Update: Orphan Drug Designations, Gene Editing Breakthroughs,…


Rare Disease news

Rare Diseases Weekly News - May 29th 2025

🔬 Rare Diseases Update: Orphan Drug Designations, Gene Therapies, Diagnostic…


Rare Disease news

Rare Diseases Weekly News - May 22nd 2025

🔬 Rare Diseases Update: CRISPR Therapy, SCA, ENPP1 Deficiency, Gene Therapy…


Rare Disease news

Rare Diseases Weekly News - May 15th 2025

🔬 Discover the latest breakthroughs in rare disease research from this week’s…


Privacy Preference Center